RNA Discoveries and Therapeutics Conference Spans Discovery to Clinical Trials
This rna discoveries and therapeutics conference convened May 30–31, 2025, in Jacksonville, Florida, bringing together experts in RNA biology and RNA therapeutics development. Sessions covered RNA-targeting compounds, RNA metabolism disruption in neurodegeneration, antisense oligonucleotide (ASO) candidate design, and RNA nano-vaccines for cancer. Industry and academic faculty from Mayo Clinic, Moderna, Johns Hopkins, and MD Anderson Cancer Center addressed gaps and opportunities in translating RNA therapeutics from discovery to clinical trials.
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2Conference Days
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30+Faculty Speakers
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2025Conference Year
Inside this resource
RNA Metabolism & Neurodegeneration
Disruption of RNA metabolism in neurodegeneration and pathways to treatment, presented by Don W. Cleveland.
RNA Therapeutics for Cancer
Clinical translation of therapeutic RNA nano-vaccines for cancer, presented by Natalie Silver.
From Discovery to Clinical Trials
Advances in translating RNA therapies to the clinic, including the Moderna experience and ASO candidate design.
RNA Data Analytics & Rare Disease
Data analytics approaches for RNA therapy design and industrializing non-profit ASO treatment for rare disease patients.
Who this serves
- Physicians in oncology, neurology, and rare disease specialties — Course directly addresses RNA-based therapeutic advances in these disease areas.
- Researchers in RNA biology and therapeutics development — Gain insight into discovery, translation, and clinical trial pathways for RNA therapies.
- Clinical trial coordinators — Learn about emerging RNA therapeutic modalities entering clinical development.
Faculty & syllabus
Faculty 5 speakers
Named conference faculty (as credited in the source program):
- Nilüfer Ertekin-Taner, MD, PhD — Mayo Clinic RNA Program
- Blanton Tolbert, PhD — Discovery of RNA-Targeting Compounds
- Don W. Cleveland, PhD — RNA Metabolism Disruption in Neurodegeneration
- Natalie Silver, MD — RNA Nano-Vaccines for Cancer
- Patrick Finn, PhD — RNA Therapeutics: Moderna Experience
Before you buy
What does the Mayo Clinic RNA Discoveries and Therapeutics Conference cover?
It covers RNA biology and RNA therapeutics development across neurological disease, cancer, and rare disease, from target discovery through translation and clinical trials, held May 30–31, 2025.
Who should attend this RNA therapeutics conference?
Physicians and healthcare providers in oncology, neurology, and metabolic specialties, along with cancer and neurological researchers, RNA-therapeutics developers, and clinical trial coordinators.
The chart
| Format | Videos |
|---|---|
| Duration | 2 Days (May 30–31, 2025) |
| Faculty | Nilüfer Ertekin-Taner, MD, PhD and conference faculty |
| Year | 2025 |
| Publisher | Mayo Clinic |
| Department | Neurology |
| Delivery | Instant download after checkout · lifetime re-access |
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